canonical disease area

Neuromuscular Disorders
Intelligence

Neuromuscular Disorders intelligence: 37 indexed trials, 13 recruiting studies, 34 sponsors across 35 countries.

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37Indexed trials
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13Recruiting
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34Sponsors
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35Countries

Leading sponsors

Hoffmann-La Roche30 recruiting
Italfarmaco21 recruiting
AskBio Inc11 recruiting
Beth Israel Deaconess Medical Center10 recruiting
BioMarin Pharmaceutical10 recruiting
Biogen10 recruiting
Catholic University of the Sacred Heart10 recruiting
Catalyst Pharmaceuticals, Inc.11 recruiting
Charitable Foundation Children with Spinal Muscular Atrophy10 recruiting
Copenhagen University Hospital, Rigshospitalet10 recruiting
Fredrik Piehl10 recruiting
Barts & The London NHS Trust10 recruiting

Geographic activity

United States22trials
United Kingdom16trials
Italy16trials
France14trials
Germany14trials
Spain14trials
Belgium13trials
Canada12trials
Japan10trials
Poland8trials
Australia8trials
Netherlands7trials

Leading interventions

Amondys 451trials
Ataluren1trials
Direct current stimulation of cervical spinal cord1trials
Drisapersen1trials
Efgartigimod PH20 SC1trials
Exondys 511trials
Flavocoxid1trials
Givinostat1trials
IVR platform trial1trials
Idebenone1trials
KL13331trials
AB-1009 (GAA Gene)1trials

Methodology note

This entity is derived from structured ClinicalTrials.gov conditions and/or MeSH normalization. Counts reflect the current NeuroRisk indexed corpus and are not guaranteed exhaustive global totals.